Protocol 
Retroviral Mediated Transfer of the cDNA for Human 
Glucocerebrosidase into Hematopoietic Stem Cells of Patients 
with Gaucher Disease 
Protocol GTI 0101 
Sponsored by: 
Genetic Therapy, Inc 
Gaithersburg, MD 
Study Co-investiaators : 
Stefan Karlsson, M.D., Ph.D Donald Kohn, M.D. 
National Institutes of Health Childrens Hospital of LA 
Cynthia Dunbar, M.D. 
National Institutes of Health 
[786] 
Recombinant DNA Research, Volume 17 
