Gene Therapy for CF using Canonic Liposome Mediated Gene Transfer: Phase I Trial 
m.E. APPENDICES 
3. REFERENCES 
1. Boat, TF, MJ Welsh and AL Beaudet. 1989. Cystic fibrosis. In The Metabolic Basis of 
Inherited Disease . AL Beaudet, WS Sly, D Valle, JB Stansbury, JB Wyngaarden and DS 
Fredrickson, editors. McGraw-Hill Information Services Company, New York. 2649- 
2680. 
2. Riordan, JR, JM Rommens, BT Kerem, N Alon, R Rozmahel, Z Grzelczak, J Zielenski, 
S Lok, N Plavsic, JL Chou, ML Drumm, MC Iannuzzi, FS Collins and LC Tsui. 1989. 
Identification of the cystic fibrosis gene: Cloning and characterization of complementary 
DNA. Science, 245:1066-1073. 
3. Rommens, JM, MC Iannuzzi, BT Kerem, ML Drumm, G Melmer, M Dean, R 
Rozmahel, JL Cole, D Kennedy, N Hidaka, M Zsiga, M Buchwald, JR Riordan, LC 
Tsui and FS Collins. 1989. Identification of the cystic fibrosis gene: Chromosome 
walking and jumping. Science, 245:1059-1065. 
4. Kerem, BT, JM Rommens, JA Buchanan, D Markiewicz, TK Cox, A Chakravarti, M 
Buchwald and LC Tsui. 1989. Identification of the cystic fibrosis gene: Genetic analysis. 
Science, 245:1073-1080. 
5. Frizzell, RA. 1987. Cystic fibrosis: A disease of ion channels? TINS, 10:190-193. 
6. Welsh, MJ. 1990. Abnormal regulation of ion channels in cystic fibrosis epithelia. 
FASEB J, 4:2718-2725. 
7. Tsui, LC. 1991. Probing the basic defect in cystic fibrosis. Current Opinion in Genetics 
and Development, 1:4-10. 
8. Bear, CE, C Li, N Kartner, RJ Bridges, TJ Jensen, M Ramjeesingh and JR Riordan. 
1992. Purification and functional reconstitution of the cystic fibrosis transmembrane 
conductance regulator (CFTR). Cell, 68:809-818. 
9. Drumm, ML, HA Pope, WH Cliff, JM Rommens, SA Martin, LC Tsui, FS Collins, RA 
Frizzell and JM Wilson. 1990. Correction of the cystic fibrosis defect in vitro by 
retrovirus-mediated gene transfer. Cell, 62:1227-1233. 
10. Rich, DP, MP Anderson, RJ Gregory, SH Cheng, S Paul, DM Jefferson, JD McCann, 
KW Klinger, AE Smith and MJ Welsh. 1990. Expression of cystic fibrosis transmem- 
brane conductance regulator corrects defective chloride channel regulation in cystic 
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